STAT+: Sickle cell gene therapies could be cost-effective even if priced as high as $1.9 million

The pending arrival of the treatments is causing a degree of trepidation, because gene therapies are so costly.

Apr 13, 2023 - 20:00
STAT+: Sickle cell gene therapies could be cost-effective even if priced as high as $1.9 million

As the U.S. health care system prepares for expensive gene therapies, a preliminary analysis suggests that a pair of forthcoming treatments for sickle cell disease would be cost-effective if priced as high as $1.9 million, depending upon certain variables.

The medications — one is being developed by Bluebird Bio and the other by a partnership between Vertex Pharmaceuticals and CRISPR Therapeutics — have not yet been approved by the Food and Drug Administration. As a result, pricing has not been disclosed, but analyst estimates have suggested the treatments may be priced at roughly $2 million.

Continue to STAT+ to read the full story…

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