Gene therapy death was caused by an unknown risk of the virus used, study suggests
“I don’t think it was foreseeable,” a gene therapy researcher says about the death of a Duchenne muscular dystrophy patient who had received a CRISPR therapy.
Last October, a 27-year-old man with Duchenne muscular dystrophy died after receiving a CRISPR-based treatment custom built to treat his particular genetic mutation.
Results of a detailed investigation released on Wednesday suggest that the patient, Terry Horgan, likely died of a previously undocumented adverse effect of the virus used to deliver the CRISPR machinery to his cells.
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